Amicus Therapeutics Leads the Way in Advanced Therapies

Amicus Therapeutics, Inc. is a biopharmaceutical company based in New Jersey. It is a leading company in the field of advanced therapies and treats a wide range of rare and orphan diseases. It deals specifically with conditions known as lysosomal storage disorders. Its product development pipeline is primarily based on the Chaperone-advanced replacement Therapy (CHART) and Enzyme Replacement Therapies (ERT).

Amicus Therapeutics boasts of having the broadest range of small molecule pharmacological chaperones in the industry. Its most significant product is known as migalastat which is a personalized medicine that can treat Fabry disease based on genetic diagnosis. Another late-stage development product in Amicus Therapeutics product pipeline is SD-101 which is a potential first-to-market therapy used to treat the rare genetic connective tissue disorder Epidermolysis Bullosa.

In the recent past, the company has collaborated with GlaxoSmithKline and JCR Pharmaceutical to investigate the coformulation with recombinant alpha-galactosidase. Amicus Therapeutics does not have manufacturing capability and mostly relies on contract manufacturing. The company has been able to expand its location in New Jersey to another research site in San Diego. It has been receiving a string of grants to help it support its studies. View the market summary of Amicus Therapeutics at finance.google.com.

In 2010. It received $0.5 million grant from the Michael J. Fox-Foundation for studies that it was doing in collaboration with the David Geffen School of Medicine at UCLA. It also received additional funds from the Alzheimer Drug Discovery Foundation in support of pre-clinical work it was undertaking together with Icahn School of Medicine at Mount Sinai.

Read: http://www.gcreport.com/amicus-therapeutics-announces-new-drug-application/

In 2013, Amicus Therapeutics was able to acquire Callidus Biopharma together with its intellectual property and proprietary materials for the enzyme replacement therapy treatment of the Pompe disease. This development was a major milestone for the company which made it stamp its authority as a leading biotechnology company in the industry. Read the company profile at Crunchbase.

Dr. Jennifer Walden Can Not Be Stopped

Dr. Jennifer Walden is a board-certified plastic surgeon in Austin, Texas. Born to parents with a passion for helping others, she found herself dreaming of a career in the medical field. So, it came as no surprise to her family when she graduated high school and earned an undergraduate degree in biology. Shortly after, Dr. Walden applied to medical school at the University of Texas Medical Branch where she was initially waitlisted. Determined to achieve her goal, she remained optimistic, and soon graduated salutatorian of her class.

After medical school, Walden was offered a spot in the Manhattan Eye, Ear, and Throat fellowship program, where she worked under the supervision of some of the most successful plastic surgeons in the industry. She remained at the hospital for nearly eight years before deciding to explore the world of entrepreneurship. With the help of her mentor Sherrell Aston, she successfully opened her owned practice right in the big apple.

Always focused on reaching her goals, Dr. Walden admits that marriage and family were not at the top of her priority list. As the majority of her early years were spent chasing her dreams, family planning just didn’t seem to fit in her plan. Now a successful business woman and plastic surgeon, Dr. Walden realized she was ready to become a mother. With no prospects for marriage, and feeling the pressure to race against time, she began to explore other options for conception.

After three rounds of IVF, Dr. Walden successful conceived. In 2011, she became the proud mother of two beautiful twin boys, Houston and Rex. Having a desire to raise her children in the same close-knit family environment she was raised in, she packed up her sons, closed her practice, and returned to Austin. With the help of a strong and encouraging support system, Dr. Walden opened a new practice in her hometown, where she continues to live out her dream.

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